“I dream about the day she will call me dad”

Milestones in the progress of Research

1999

Mutations in the MECP2 gene in the X chromosome are discovered to be the cause of Rett syndrome

Researchers are developing a model of Rett mice and research begins in mice

2001
2007

A breakthrough: Rett syndrome is reversible in mouse models!

Clinical studies on Rett girls are starting for the first time in the world

2012
2013

Genetic therapy in laboratory mice has cured the mice

Clinical trials are underway

2016
2017

A three-year plan to cure the syndrome began

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